Read the latest positive news, breakthroughs, and inspiring stories about neurofibromatosis, curated daily by BrightWire.
A nonprofit foundation is turning abandoned pharmaceutical treatments into life-saving therapies for children with rare diseases. Their first rescued drug just won FDA approval and sparked a $3.4 billion acquisition.
Years of tireless fundraising by teacher's aide Zoe Petropoulos and her family have helped fuel a breakthrough that could transform treatment for a genetic disorder affecting thousands. The discovery could lead to treatments as simple as probiotics.
Billionaire Dan Gilbert is pouring $50 million yearly into rare disease research after losing his son Nick to neurofibromatosis. His foundation has already helped create the first FDA-approved treatments for the incurable genetic disorder.
After losing his oldest son Nick to neurofibromatosis, billionaire Dan Gilbert is pouring $50 million annually into research for the rare disease that affects 170,000 Americans. The Gilbert Family Foundation has turned grief into action, raising $12 million in a single night while creating lasting tributes that keep Nick's memory alive.