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6990 results for "fda-approved therapy"
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Children as young as two can now receive a groundbreaking gene therapy that offers a potential cure for sickle cell disease. The FDA's approval of Casgevy marks a historic expansion that could prevent irreversible damage before it starts.
Children born deaf are now hearing their mother's voice for the first time, thanks to a groundbreaking gene therapy that restores natural hearing. The FDA just approved the treatment, and the company is offering it completely free across the United States.
Children born with a specific type of genetic hearing loss can now hear their parents' voices and dance to music, thanks to the FDA's approval of the first-ever gene therapy for inherited deafness. The one-time treatment helps patients avoid cochlear implants and restores natural hearing.
Children as young as 2 can now access a breakthrough gene therapy that could eliminate the need for lifelong blood transfusions. The FDA just expanded approval of Casgevy, a one-time CRISPR treatment that edits a patient's own cells to fight sickle cell disease.
Children born deaf from a genetic mutation can now hear naturally thanks to a groundbreaking gene therapy just approved by the FDA. The one-time treatment restores a missing protein in the inner ear, allowing sound signals to reach the brain.
Children born with a life-threatening immune disorder now have hope thanks to a newly approved gene therapy that could save their lives with a single treatment. The FDA just greenlit Kresladi, a breakthrough for severe LAD-1 that leaves kids defenseless against infections.
The FDA just approved the first gene therapy to treat genetic hearing loss, giving hope to dozens of families each year whose babies are born deaf. Even better? The company is making it free for all U.S. patients.
Children and adults with a rare genetic disease that required eating every few hours can now receive a one-time gene therapy treatment. The FDA approval marks the first treatment to address the root cause of glycogen storage disease type Ia.
A groundbreaking gene therapy just won FDA approval for children born deaf from a rare genetic condition. Kids who once moved their lips silently are now hearing their own voices for the first time.
Children and adults with a rare genetic disorder that forced them to eat cornstarch every few hours just got their first real treatment option. The FDA approved a one-time gene therapy that could free up to 2,500 Americans from a relentless routine that meant any missed dose risked seizures or death.
A groundbreaking gene-editing treatment could reach patients faster than ever before, as Prime Medicine asks the FDA to approve their therapy after just two successful treatments. The drug uses a revolutionary CRISPR technique to fix a genetic disorder that leaves patients vulnerable to deadly infections.
The FDA just approved a groundbreaking clinical trial that could actually reverse aging at the cellular level. Scientists will test whether they can reset human cells to a younger state, bringing one of medicine's biggest theories out of the lab and into real patients.
A one-week-old baby received groundbreaking gene therapy for a fatal disease just days after FDA approval, transforming what doctors once called a "death sentence" into a life full of possibility. Today, 10-month-old Samuel is crawling, smiling, and showing no signs of the disease that would have confined him to a wheelchair.
A groundbreaking depression treatment using psilocybin is showing promising results in clinical trials, potentially becoming the first psychedelic therapy approved by the FDA. Two major studies confirm the compound helps patients with severe depression find relief.
A groundbreaking cell therapy has successfully treated stiff person syndrome, a rare neurological disorder that causes severe muscle stiffness and mobility problems. If approved by the FDA this summer, it would become the first treatment for the condition and the first personalized CAR-T therapy for any autoimmune disease.
A revolutionary gene therapy just restored hearing to children born completely deaf, and the company is giving it away for free in the U.S. Two-year-old Travis Smith, who never heard his name, now jams out to Bruno Mars.
The FDA reversed course on a groundbreaking gene therapy for Huntington's disease, bringing new hope to thousands of families. The treatment from biotech company UniQure can now move forward toward U.S. approval.
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A groundbreaking gene therapy now offers hope to children born with a rare form of deafness, with 80% of trial participants gaining significant hearing within a year. Even better, the maker plans to provide it free to U.S. patients.
A groundbreaking gene therapy that restored hearing in deaf children just won FDA approval and will be offered free to eligible Americans. The treatment marks the first cure for a rare genetic form of deafness that previously required lifelong cochlear implants.
Adults with a rare form of lung cancer now have a new treatment option after their disease stops responding to initial therapies. The FDA just approved zidesamtinib for patients with ROS1-positive lung cancer who've already tried one targeted treatment.
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