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4599 results for "genetic therapy"
Children born deaf from a genetic mutation can now hear naturally thanks to a groundbreaking gene therapy just approved by the FDA. The one-time treatment restores a missing protein in the inner ear, allowing sound signals to reach the brain.
The FDA just approved the first gene therapy to treat genetic hearing loss, giving hope to dozens of families each year whose babies are born deaf. Even better? The company is making it free for all U.S. patients.
Two Philadelphia research teams just received millions in federal funding to develop one-dose gene therapies that could cure rare genetic diseases within five years. The breakthrough approach uses AI and new delivery methods to create treatments that work for multiple patients instead of requiring custom therapy for each person.
University of Toronto researchers engineered a breakthrough RNA treatment that could tackle thousands of genetic diseases with a single approach. The therapy teaches cells to ignore faulty "stop signals" that prevent life-saving proteins from forming.
A breakthrough gene therapy has revolutionized how Canadian doctors approach ALS testing. Now 100% of physicians offer genetic testing to all patients, regardless of family history.
Pharmaceutical giant Eli Lilly is ramping up its efforts to develop gene therapies that could restore hearing in people with genetic hearing loss. The move signals growing confidence in cutting-edge treatments that address the root causes of deafness.
Children born with epidermolysis bullosa, a painful genetic disorder causing skin to blister at the slightest touch, now have real treatment options for the first time. Three new FDA-approved therapies are healing wounds that doctors could only bandage before.
A newly approved ALS treatment can now target specific genetic causes of the disease, offering hope to patients with Lou Gehrig's disease. The FDA fast-tracked the therapy, marking a significant breakthrough in personalized medicine for neurological conditions.
A Louisiana man just became the first person in the state to be functionally cured of sickle cell disease using advanced gene therapy. The breakthrough offers hope to thousands living with the painful genetic blood disorder.
Twenty-seven out of 28 patients with severe sickle cell disease are now living pain-free after a groundbreaking gene editing treatment. The one-time therapy is offering new hope to people living with a genetic disorder that typically shortens life expectancy to the mid-40s.
Scientists have begun testing a breakthrough gene therapy that could restore hearing for people with the most common genetic cause of deafness. Skylark Bio just dosed their first patient, marking a major step toward helping millions born with this genetic mutation.
Scientists are building a system to make life-saving gene therapy accessible to the 400 million people living with rare diseases worldwide. The new Center for Therapeutic Genetics wants to turn custom genetic medicine into a standardized procedure that can help patient after patient.
Volunteer therapy dogs are making rounds at WellSpan hospitals, bringing comfort and smiles to patients, families, and healthcare workers during their toughest days. One patient who hadn't spoken in five years after a car accident tried to talk when a therapy dog laid its head on her shoulder.
Scientists discovered a therapy that helps brain cells bypass genetic damage instead of fixing it, opening new hope for treating conditions like schizophrenia and autism. The approach works like taking a detour around fallen trees rather than clearing the original road.
Virginia Tech researchers discovered a therapy that helps brain cells bypass genetic damage rather than repair it, opening new doors for treating conditions linked to schizophrenia and autism. The experimental treatment restored healthy brain development in mice by taking an alternate cellular route.
Scientists at MD Anderson have discovered two genetic markers that predict which prostate cancer patients will respond to an emerging therapy called ferroptosis. The breakthrough could help doctors quickly match resistant cancers to the right treatment.
Scientists created a breakthrough treatment that successfully restored missing muscle protein in models of Duchenne muscular dystrophy, dramatically improving strength and endurance without the dangerous side effects of current therapies. The new approach could transform treatment for rare genetic disorders and beyond.
A Pennsylvania baby born with a deadly genetic disorder is now thriving after doctors created the world's first personalized CRISPR treatment just for him. Baby KJ can now eat protein and has stopped all medications after three doses of the groundbreaking therapy.
A therapist noticed runners open up more easily while moving, sparking a growing trend in outdoor therapy sessions. Walk-and-talk therapy combines mental health support with the proven benefits of nature and exercise.
Two scientists just won a $3 million prize for discovering how to switch on healthy blood cells in people with sickle cell disease. Their breakthrough has led to gene therapies that functionally cure patients who once faced lifelong pain.
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