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38 results for "pediatric health"
A common blood pressure medication combined with chemotherapy is safely treating children with aggressive bone cancer. Nine young patients have tolerated the treatment well, with early signs their immune systems are fighting back.
A rare muscle disease that once offered families almost no hope now has multiple new treatments helping kids stay stronger longer. Gene therapies and innovative medications are changing what's possible for children with Duchenne Muscular Dystrophy.
A breakthrough medication could become the first FDA-approved treatment designed specifically for children with Tourette syndrome, reducing tics by 50% without the harsh side effects of current drugs. After a successful Phase III trial across 77 sites, the drug ecopipam is heading for FDA review.
Children born with epidermolysis bullosa, a painful genetic disorder causing skin to blister at the slightest touch, now have real treatment options for the first time. Three new FDA-approved therapies are healing wounds that doctors could only bandage before.
A Kansas City hospital will multiply its capacity to deliver breakthrough cell and gene therapies that can cure diseases with a single treatment. The expansion promises to bring life-changing care closer to home for families across the Midwest.
Boys living with Duchenne muscular dystrophy in England now have access to a new treatment that could extend their ability to walk by up to five years. The NHS has approved givinostat, offering fresh hope to families facing this devastating muscle-wasting disease.
A promising treatment for microvillus inclusion disease, a deadly childhood condition, has entered breakthrough therapy talks with the FDA. The oral medication has already shown it can reduce life-sustaining interventions in young patients.
A boy born with a life-threatening heart defect is now the face of hope for thousands walking to fight heart disease. The Engles family turned their son's medical journey into a mission to save other lives.
A decades-old medicine originally used for African sleeping sickness is giving new hope to families battling Bachmann-Bupp syndrome, one of the world's rarest genetic diseases. Just 20 people worldwide have been diagnosed, but five patients are already showing visible improvements.
A decades-old medication is giving hope to children with Bachmann-Bupp syndrome, a genetic disorder affecting only 20 people worldwide. Early treatments show the drug may ease severe symptoms by targeting the root cause.
Chinese scientists successfully treated children born deaf by delivering a missing gene directly into their inner ear cells. All patients under age 3 can now hear everyday conversations after a single treatment.
UnityPoint Health in Dubuque now offers a specialized physical therapy program that helps young people with scoliosis avoid surgery. The first program of its kind in the tri-state area gives local families access to treatment that previously required traveling to Iowa City, Chicago, or beyond.
Two-year-old Travis Smith was born deaf, but a groundbreaking gene therapy treatment has given him the gift of sound. Now he can hear his mother's voice and dance to music for the first time.
A hospital in Kenya is hosting a nationwide charity run to fund heart surgeries for 450 children who desperately need cardiac care. The May event will expand to 11 counties, bringing lifesaving treatment closer to families across the nation.
Children born completely deaf are hearing whispers for the first time thanks to an experimental gene therapy that has shown remarkable success in the largest study of its kind. The treatment could become the first FDA-approved gene therapy for deafness within months.
A Stanford study found the Apple Watch captured twice as many heart rhythm problems in children as traditional medical monitors. The breakthrough could make heart care more accessible for millions of young patients.
Children born deaf are now hearing and speaking for the first time, thanks to a breakthrough gene therapy that reversed a rare inherited form of deafness. The treatment's effects have lasted up to 2.5 years, the longest follow-up yet reported.
Pharmaceutical company Roche announced a new clinical trial that could bring a life-changing gene therapy for Duchenne muscular dystrophy to young patients across Europe. The move comes after extensive feedback from families and regulators who want to see this treatment option become available.
Children with eosinophilic esophagitis now have more treatment options than ever, including a convenient at-home injection and monitoring tools that don't require sedation. These advances are making life easier for families managing this chronic digestive condition.
A new gene therapy has reduced seizures by up to 85% in children with Dravet syndrome, a devastating form of epilepsy that begins in infancy. Kids in the trial are not only having fewer seizures but are making friends and enjoying life alongside their peers for the first time.
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