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21 results for "pediatric health"
Pharmaceutical company Roche announced a new clinical trial that could bring a life-changing gene therapy for Duchenne muscular dystrophy to young patients across Europe. The move comes after extensive feedback from families and regulators who want to see this treatment option become available.
Children with eosinophilic esophagitis now have more treatment options than ever, including a convenient at-home injection and monitoring tools that don't require sedation. These advances are making life easier for families managing this chronic digestive condition.
A new gene therapy has reduced seizures by up to 85% in children with Dravet syndrome, a devastating form of epilepsy that begins in infancy. Kids in the trial are not only having fewer seizures but are making friends and enjoying life alongside their peers for the first time.
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A Colorado scientist's breakthrough research is transforming treatment for children with a devastating rare disease, bringing relief after years of pain. Two patients are already showing remarkable improvement from a new therapy approach.
A girl battling a brain tumor is finding every Kirsty in the world to join her mission funding cancer research. She's already connected with 1,000 Kirstys across the globe and raised £120,000.
Four major health systems in Kansas City are creating one of the nation's first fully integrated theranostics centers, bringing cutting-edge precision cancer treatment to children for the first time. The groundbreaking collaboration will make the region a national destination for less invasive, more targeted cancer care.
Scientists at Texas Children's Hospital discovered a promising way to treat Rett syndrome, a rare disorder that affects 1 in 10,000 girls and currently has no cure. The breakthrough could help 65% of patients by boosting levels of a partially working protein in their brains.
A Georgia brewpub packed with cowboy boots and country music raised vital funds for families battling pediatric cancer. The Sebi-Strong Foundation, started by childhood brain cancer survivor Sebastian Tran, now helps other families through their toughest days.
Researchers in South Africa are studying children born with HIV to find ways they could live without daily medication. Early treatment might help their young immune systems control the virus naturally.
A groundbreaking study in KwaZulu-Natal is treating babies with HIV within 21 days of birth, giving science its best shot at understanding how to defeat the virus. The research proves that hope works best when paired with honesty and real community partnership.
Researchers in South Africa are pioneering ethical trials that could lead to HIV remission in children who started treatment at birth. The groundbreaking work centers African voices and puts kids' safety first.
A tiny pacemaker smaller than a grain of rice can now save babies born with heart defects without risky removal surgery. The device dissolves naturally after seven critical days of healing.
A breakthrough study from Sweden shows that giving extremely premature babies early hydrocortisone treatment dramatically increases their chances of surviving without lifelong lung disease. The simple, safe treatment could help thousands of the tiniest patients worldwide.
Around 20 people in England with a debilitating genetic condition can now access the first treatment that targets the root cause of their disease. The NHS will provide pegzilarginase to patients with arginase-1 deficiency after breakthrough approval.
Children with broken femurs are getting dramatically better pain relief in emergency rooms, thanks to an ultrasound-guided procedure that slashes opioid use by nearly three-quarters. A groundbreaking study shows the targeted nerve blocks work better than traditional treatment without any added risks.
A Wellington baby may be the only person on Earth with his specific genetic condition, but his parents' determination and medical breakthroughs are giving him a fighting chance. One year after his diagnosis, Archie Eaton is finally gaining weight and reaching new milestones.
Scientists prevented a life-threatening brain condition in newborn mice using RNA therapy, reducing cases by 67%. The breakthrough could spare thousands of babies from risky brain surgery each year.
Virginia Tech researchers discovered early brain changes in Leigh syndrome that could help doctors identify affected children months before symptoms appear. The breakthrough offers hope for earlier treatment of this devastating genetic disorder.
A gene therapy called ELEVIDYS is helping young boys with Duchenne muscular dystrophy maintain their ability to walk, run, and stand years after a single treatment. Three years after receiving the therapy, treated children showed 70% less decline in muscle function compared to untreated children.
Stroke care just took its biggest leap forward in a decade, with new guidelines expanding who can receive advanced treatments and offering the first-ever recommendations for treating strokes in children. Nearly 800,000 Americans have a stroke each year, making this update potentially life-changing for thousands of families.
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