Find uplifting stories about heroes, innovations, and solutions
4 results for "** gene therapy"
Philadelphia researchers just won the prestigious 2026 Breakthrough Prize for developing a gene therapy that restores vision in children born with a rare form of blindness. The treatment has already helped hundreds of patients see for the first time.
Five people with beta thalassemia no longer need regular blood transfusions after receiving a groundbreaking gene therapy treatment developed in China. Their recovery marks a major milestone in making cutting-edge genetic medicine accessible worldwide.
A Louisiana man with lifelong sickle cell disease received groundbreaking gene therapy that eliminated his symptoms and opened the door to his dream career as a pilot. His story represents hope for thousands living with this painful genetic condition.
After becoming the first country to approve a revolutionary gene-editing therapy in 2023, the UK is now using Casgevy to treat patients with sickle cell disease and β-thalassaemia. The treatment has shown remarkable results, freeing 97% of sickle cell patients from painful episodes for over a year.