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6976 results for "sickle cell disease"
A new stem cell transplant developed at Johns Hopkins has cured sickle cell disease in 95% of patients, using half-matched donors like parents or siblings. The breakthrough means nearly every sickle cell patient can now access a cure that also preserves fertility.
Daniel Cressy just became the first person on the Gulf Coast functionally cured of sickle cell disease through gene therapy, clearing the path to his dream of becoming a commercial pilot. His groundbreaking treatment offers new hope for Louisiana, which has the highest rate of sickle cell disease in America.
A 41-year-old mother who spent her life battling sickle cell disease just became the first adult in Maryland to receive a potentially curative gene therapy using her own cells. After decades of hospital stays and missing family moments, Jessica Ceja now has hope for a life without the painful disease.
Jessica Ceja became the first person in Maryland to receive groundbreaking gene therapy that could cure her lifelong sickle cell disease. Her own cells were reengineered in a lab to produce healthy red blood cells, potentially ending decades of pain.
Children with sickle cell disease now have a survival rate exceeding 95% thanks to breakthrough stem cell transplant techniques. New treatments are also opening curative options for kids who previously had no donor matches.
Two scientists just won a $3 million prize for discovering how to switch on healthy blood cells in people with sickle cell disease. Their breakthrough has led to gene therapies that functionally cure patients who once faced lifelong pain.
Daniel Cressy, 23, has become the first person in Louisiana to be functionally cured of sickle cell disease using groundbreaking gene therapy. His treatment gives hope to over 100,000 Americans living with the painful blood disorder.
A Louisiana man just became the first person in the state to be functionally cured of sickle cell disease using advanced gene therapy. The breakthrough offers hope to thousands living with the painful genetic blood disorder.
After decades of research, gene therapy is bringing lasting relief to sickle cell patients after just one treatment. UCLA researchers are leading the charge to cure a disease that affects 100,000 Americans.
A 13-year-old Nashville boy just completed groundbreaking gene-editing treatment that could potentially cure his sickle cell disease. Rickey Buggs became the first commercial patient at his hospital to receive the therapy, offering hope to 100,000 Americans living with the condition.
Physicians have reached a remarkable 95% cure rate for sickle cell disease using bone marrow transplants, offering new hope to millions living with this painful genetic condition. This breakthrough represents a major leap forward in treating a disease that has long been considered incurable.
Two researchers just won a $3 million Breakthrough Prize for discoveries that led to gene therapies functionally curing sickle cell disease and beta-thalassemia. Their work identified a genetic switch that helps patients' bodies produce healthy blood cells again.
A breakthrough gene editing treatment has achieved what doctors call a "functional cure" for sickle cell disease, with 27 out of 28 patients experiencing zero painful crises after receiving the therapy. The one-time treatment edits patients' own blood cells to correct the genetic mutation, offering new hope for 100,000 Americans living with this painful disease.
A Maryland mother who spent years in and out of hospitals every month is now living pain-free after becoming the first woman in her state to receive groundbreaking gene therapy for sickle cell disease. Clinical trials show up to 93% of patients stopped experiencing severe pain crises.
A single gene-editing treatment has freed nearly all trial patients from the crushing pain crises that define sickle cell disease. Doctors are calling it a functional cure that uses patients' own cells to rewrite their future.
Nemours Children's Hospital in Wilmington can now offer a groundbreaking one-time gene therapy that could give children with sickle cell disease a chance at a transformed life. The FDA-approved treatment addresses the root genetic cause of the disease that affects 100,000 Americans and shortens life expectancy by more than 20 years.
Victoria Hospital in Kisumu has become Kenya's first public facility to offer automated red blood cell exchange therapy for sickle cell patients. The specialized machine offers hope to thousands in western Kenya, where the disease is highly prevalent.
Children as young as 2 can now access a breakthrough gene therapy that could eliminate the need for lifelong blood transfusions. The FDA just expanded approval of Casgevy, a one-time CRISPR treatment that edits a patient's own cells to fight sickle cell disease.
A foundation leader living with sickle cell disease is championing a plan to teach students about the genetic condition before they start families. The comic strip education model has already shown success in pilot programs across Ghana.
A discovery about baby blood just transformed life for sickle cell patients forever. Two researchers won the "Oscars of Science" for finding the switch that could cure a painful disease affecting millions.
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