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3 results for "duchenne muscular dystrophy"
A Staten Island father is leading 15 runners through 80 miles of Arizona desert to fund a cure for the disease affecting his 16-year-old son. JAR of Hope has taken teams around the world to raise money for Duchenne muscular dystrophy research.
Boys with Duchenne muscular dystrophy are showing sustained improvements three years after receiving Elevidys gene therapy, demonstrating the treatment can slow progression of this muscle-wasting disease. The results offer hope to families facing a condition that typically causes rapid physical decline around age 9.
A gene therapy called ELEVIDYS is helping young boys with Duchenne muscular dystrophy maintain their ability to walk, run, and stand years after a single treatment. Three years after receiving the therapy, treated children showed 70% less decline in muscle function compared to untreated children.