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9166 results for "genetic treatment"
A newly approved ALS treatment can now target specific genetic causes of the disease, offering hope to patients with Lou Gehrig's disease. The FDA fast-tracked the therapy, marking a significant breakthrough in personalized medicine for neurological conditions.
Scientists at MD Anderson have discovered two genetic markers that predict which prostate cancer patients will respond to an emerging therapy called ferroptosis. The breakthrough could help doctors quickly match resistant cancers to the right treatment.
Children born with epidermolysis bullosa, a painful genetic disorder causing skin to blister at the slightest touch, now have real treatment options for the first time. Three new FDA-approved therapies are healing wounds that doctors could only bandage before.
Doctors are catching ovarian cancer earlier and keeping it away longer with personalized treatments and genetic testing. These advances are giving patients real hope where there was once only uncertainty.
After nearly a decade on the same anxiety medication, former pageant titleholder Madeline Bohlman discovered a genetic test that changed everything. The GeneSight test revealed how her DNA affects medication response, leading to treatment that finally worked.
People with a rare genetic disorder that causes dangerous fat buildup in their blood now have a breakthrough treatment that cuts triglyceride levels by nearly a third. The UK just approved olezarsen for adults with familial chylomicronemia syndrome, a condition that can trigger life-threatening pancreas inflammation.
Around 20 people in England with a debilitating genetic condition can now access the first treatment that targets the root cause of their disease. The NHS will provide pegzilarginase to patients with arginase-1 deficiency after breakthrough approval.
Scientists at Newcastle and Queen Mary universities have identified genetic markers that could transform psoriasis treatment into truly personalized care. The breakthrough analyzed over 700 patient samples using AI to decode which treatments work best for individual patients.
Scientists are developing better treatments for idiopathic pulmonary fibrosis, a deadly lung disease that kills most patients within five years. Understanding the genetic and environmental causes is finally leading to hope for the 3 million people affected worldwide.
A Fort Worth 19-month-old with a deadly genetic condition is now walking, thanks to becoming the first child in Texas to receive a newly approved higher-dose treatment. Jessie Gonzales was diagnosed at 7 days old with SMA type 1, which had an 8% survival rate before treatments existed.
Scientists developed technology that traces hundreds of cancer mutations back to shared control switches, potentially simplifying treatment. The breakthrough could mean one therapy targeting multiple genetic causes instead of treating each mutation separately.
Australian scientists have developed a revolutionary platform that can analyze over 100 genetic risk factors for multiple sclerosis at once. This breakthrough could lead to personalized treatments for thousands living with the unpredictable disease.
Yale researchers created a groundbreaking database of 520 FDA-approved drugs by studying tiny zebrafish, revealing potential personalized treatments for people with specific autism-related genetic mutations. One drug candidate successfully reversed disrupted behaviors in both fish and human brain cells.
Scientists at Carnegie Mellon University have discovered a precise way to target toxic RNA that causes myotonic dystrophy type 1, the most common adult-onset muscular dystrophy affecting 1 in 2,300 people worldwide. The breakthrough could lead to treatments with fewer side effects for this currently incurable disease and other devastating genetic disorders.
Scientists at UC San Diego created an AI model that reads a tumor's genetic code and predicts which treatments will work best. The breakthrough could help doctors match more cancer patients to effective therapies.
Families affected by Hunter syndrome now have hope as the FDA approves Avlayah, the first treatment designed to replace a missing enzyme that causes dangerous sugar buildup in the brain. This breakthrough marks a major victory for patients with this rare genetic disease.
Virginia Tech researchers discovered a therapy that helps brain cells bypass genetic damage rather than repair it, opening new doors for treating conditions linked to schizophrenia and autism. The experimental treatment restored healthy brain development in mice by taking an alternate cellular route.
Advanced genetic testing could eliminate the 40% higher breast cancer death rate among Black women by identifying high-risk tumors that standard tests miss. Gene profiling tools are helping doctors create personalized treatment plans that work equally well across racial groups.
Scientists discovered a way to use tiny zebrafish to quickly test if a newborn's genetic mutation will actually cause a deadly disease. The breakthrough helps doctors avoid giving babies unnecessary $2 million treatments while still protecting those who truly need help.
The FDA just approved the first treatment for Menkes disease, a rare genetic disorder that has claimed countless young lives. Copper histidinate could help babies with this devastating condition finally have a fighting chance.
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