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4672 results for "retinal disease"
Scientists at the University of Twente and Radboudumc are building a working human retina on a microchip, eliminating the need for animal testing while speeding up treatment for rare eye diseases. They've already successfully combined the first two retinal layers, something never achieved before.
Scientists at Duke University grew specialized retinal blood vessel cells from stem cells and successfully used them to restore vision in mice with damaged retinas. The breakthrough could lead to new treatments for millions suffering from diabetic retinopathy and other causes of blindness.
A groundbreaking treatment for Huntington's disease just cleared a major hurdle, bringing hope to 240,000 Americans affected by this devastating condition. The experimental therapy could become the first disease-modifying treatment for a disorder that has had none.
A groundbreaking treatment for myotonic dystrophy type 1 reduced toxic proteins by 40% and improved muscle function in patients who've never had disease-modifying options. The New England Journal of Medicine just published results that could lead to the first approved therapy for this progressive, often fatal disease.
Researchers discovered how to disguise healthy mitochondria so they can slip into diseased cells undetected, extending the lives of mice with a fatal genetic disorder. The breakthrough could one day help children born with rare mitochondrial diseases.
A new treatment for a rare kidney disease just passed a major test, bringing hope to 330,000 patients in the U.S. and Europe. Vertex's drug successfully reduced a key disease marker by half in late-stage trials.
University of Queensland researchers have developed a breakthrough drug that could transform Motor Neurone Disease from a terminal diagnosis into a manageable chronic condition within five years. The discovery unlocks a previously untargetable immune receptor that plays a key role in neurodegenerative diseases.
Pearl Jam's Eddie Vedder and Canadian director Matt Finlin created a documentary following the race to cure epidermolysis bullosa, a devastating skin disease affecting children worldwide. The Netflix film captures breakthrough research that could unlock treatments for thousands of rare diseases.
For the first time, a gene therapy has shown dramatic results in slowing Huntington's disease, offering hope to 8,000 UK families who've had no treatment options until now. Patients receiving the higher dose experienced 75% less disease progression over three years.
Four leading European research institutes have joined forces to speed up treatments for Alzheimer's, Parkinson's, and other brain diseases affecting millions. The CURE-ND Alliance brings together over 2,500 scientists working to transform how we understand and treat neurodegenerative diseases.
A Nashville family transformed their annual Kentucky Derby party into a powerful fundraiser after their daughter was diagnosed with an incurable nerve disease. Last year alone, they raised $75,000 for research into Charcot-Marie-Tooth disease.
A rice-sized implant with living cells is now FDA-approved to slow vision loss in MacTel patients, offering hope to thousands losing their sight. For the first time, people with this rare retinal disease have a real chance to preserve their independence.
Jeff Carroll learned he carried the gene for deadly Huntington's disease. Instead of giving up, he became a neuroscientist dedicated to finding a cure for the condition killing him.
After initially calling it a failed product, the FDA reversed course to allow accelerated approval of a groundbreaking gene therapy that could slow Huntington's disease. The decision brings hope to 40,000 Americans living with the fatal disorder that currently has no cure.
The FDA has accepted a groundbreaking treatment for Alexander disease for priority review, offering hope to families battling a rare neurological condition that has no approved therapies. If approved by September, zilganersen would become the first medicine ever available for this devastating illness.
The FDA reversed course on a groundbreaking gene therapy for Huntington's disease, bringing new hope to thousands of families. The treatment from biotech company UniQure can now move forward toward U.S. approval.
A promising treatment for microvillus inclusion disease, a deadly childhood condition, has entered breakthrough therapy talks with the FDA. The oral medication has already shown it can reduce life-sustaining interventions in young patients.
After eliminating trachoma and other neglected tropical diseases, Malawi is leading African nations to make disease prevention a human rights issue at the UN. Twenty-five African countries have now eliminated at least one neglected tropical disease, proving progress is possible.
NYU is solving diseases faster by throwing out the old playbook: instead of keeping scientists in separate buildings, they're mixing engineers, doctors, and AI experts into teams focused on beating specific diseases. Early wins include a startup detecting airborne pathogens and "inverse vaccines" that could cure celiac disease and allergies.
A University of Kentucky scientist is turning Lyme disease bacteria against itself in a promising new treatment approach. The breakthrough comes as tick-borne illnesses have jumped 128% nationwide since 2020.
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