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5768 results for "huntington's disease"
A groundbreaking treatment for Huntington's disease just cleared a major hurdle, bringing hope to 240,000 Americans affected by this devastating condition. The experimental therapy could become the first disease-modifying treatment for a disorder that has had none.
For the first time, a gene therapy has shown dramatic results in slowing Huntington's disease, offering hope to 8,000 UK families who've had no treatment options until now. Patients receiving the higher dose experienced 75% less disease progression over three years.
After initially calling it a failed product, the FDA reversed course to allow accelerated approval of a groundbreaking gene therapy that could slow Huntington's disease. The decision brings hope to 40,000 Americans living with the fatal disorder that currently has no cure.
The FDA reversed course on a groundbreaking gene therapy for Huntington's disease, bringing new hope to thousands of families. The treatment from biotech company UniQure can now move forward toward U.S. approval.
Families fighting Huntington's disease celebrated a breakthrough this Valentine's Day as researchers announced the first treatment for the deadly brain condition. The discovery brings renewed hope to a community that has waited decades for medical progress.
A groundbreaking gene therapy called AMT-130 has slowed Huntington's disease progression by 75% in clinical trials, offering hope to families who've waited 154 years for effective treatment. The one-time treatment could preserve patients' ability to walk, speak, and connect with loved ones for years longer.
Scientists used advanced AI to discover why Huntington's disease begins at vastly different ages in patients, finding that genetic context matters more than previously understood. The breakthrough could lead to personalized treatments for this and other hereditary diseases.
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Researchers at Berkeley Lab found a breakthrough approach to halt Huntington's disease using a simple antioxidant that repairs DNA damage in the brain. The treatment reversed symptoms in mice without complicated gene editing, offering fresh hope for patients with this fatal inherited condition.
Jeff Carroll learned he carried the gene for deadly Huntington's disease. Instead of giving up, he became a neuroscientist dedicated to finding a cure for the condition killing him.
Nancy Wexler had a 50/50 chance of developing the same fatal disease that took her mother. Instead of retreating, she spent decades in Venezuela and helped identify the gene responsible for Huntington's disease.
Latus Bio just secured $42 million to advance treatments for two devastating genetic diseases, including Huntington's. The funding brings hope to families waiting for breakthroughs in conditions that currently have no cure.
Researchers discovered how to restore movement in mice with Huntington's disease by reactivating specific brain cells, and the improvements lasted for days. This breakthrough could open new treatment paths for a disease that currently has no cure.
Scientists discovered a more precise way to fight Huntington's disease by targeting only the most toxic form of the disease protein. This breakthrough could make treatments more effective than current approaches that reduce all forms of the protein.
Jeff Carroll carries the gene for Huntington's disease, the same condition that killed his mother and grandmother. Now he's leading a $400 million initiative to find cures for brain diseases before his own symptoms progress.
Berkeley Lab researchers discovered that simple antioxidants can prevent brain cell death in Huntington's disease, opening a faster path to human trials than gene therapy. The breakthrough reveals the fatal disease attacks the brain through DNA damage, not just genetic mutations.
Scientists discovered that the toxic protein clusters blamed for Huntington's disease might actually be the brain's defense system, not the villain. This finding could transform how we treat multiple brain diseases.
When someone told a young woman she was "too close" to her family's disease to become a researcher, Jill Briceño had the perfect response. Her answer, inspired by mastering Cuban cooking, could change how we think about rare disease research.
Nancy Wexler discovered her mother's illness was hereditary and she had a 50% chance of getting it. Instead of retreating, she led the groundbreaking research that found the gene responsible for Huntington's disease.
Scientists have developed an advanced MRI technique that can detect cellular changes in Huntington's disease patients' brains while they're still alive. This breakthrough could help researchers measure whether new treatments are actually working at a cellular level.
Nancy Wexler spent 25 years hunting for the gene that caused Huntington's disease in her family. Now living with the condition herself, she's still leading research to help future generations.
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