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10 results for "huntington's disease"
Nancy Wexler spent 25 years hunting for the gene that caused Huntington's disease in her family. Now living with the condition herself, she's still leading research to help future generations.
A groundbreaking gene therapy called AMT-130 has slowed Huntington's disease progression by 75% in clinical trials, offering hope to families who've waited 154 years for effective treatment. The one-time treatment could preserve patients' ability to walk, speak, and connect with loved ones for years longer.
Nancy Wexler had a 50/50 chance of developing the same fatal disease that took her mother. Instead of retreating, she spent decades in Venezuela and helped identify the gene responsible for Huntington's disease.
When someone told a young woman she was "too close" to her family's disease to become a researcher, Jill Briceño had the perfect response. Her answer, inspired by mastering Cuban cooking, could change how we think about rare disease research.
For the first time, a gene therapy has shown dramatic results in slowing Huntington's disease, offering hope to 8,000 UK families who've had no treatment options until now. Patients receiving the higher dose experienced 75% less disease progression over three years.
Families fighting Huntington's disease celebrated a breakthrough this Valentine's Day as researchers announced the first treatment for the deadly brain condition. The discovery brings renewed hope to a community that has waited decades for medical progress.
A groundbreaking treatment for Huntington's disease just cleared a major hurdle, bringing hope to 240,000 Americans affected by this devastating condition. The experimental therapy could become the first disease-modifying treatment for a disorder that has had none.
A daily pill tested in New Zealand has stopped Huntington's disease progression in its tracks, offering families the first real hope for a condition that has had no cure. The treatment is far more practical than previous therapies that required invasive brain injections.
Country star Chase Rice will headline a benefit concert that's raised over $3.6 million for Huntington's disease research since 2011. The April event continues the legacy of Bev Hartig, who inspired a movement proving music and hope can fuel real scientific progress.
Scientists used advanced AI to discover why Huntington's disease begins at vastly different ages in patients, finding that genetic context matters more than previously understood. The breakthrough could lead to personalized treatments for this and other hereditary diseases.