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Morocco just launched a Precision Medicine Hub that will help thousands of patients with rare diseases get faster diagnoses and coordinated care. The new national center brings together advanced genetic testing, specialist teams, and patient support under one roof.
A newly approved medication could help people with Prader-Willi syndrome control the constant, overwhelming hunger that defines their daily lives. One mother shares why she's hopeful this treatment will give her son Robert a chance at greater independence and happiness.
Around 20 people in England with a debilitating genetic condition can now access the first treatment that targets the root cause of their disease. The NHS will provide pegzilarginase to patients with arginase-1 deficiency after breakthrough approval.