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598 results for "rna editing"
A 1989 Nobel Prize-winning discovery revealed RNA could perform chemistry, not just carry instructions. That breakthrough now enables mRNA vaccines, CRISPR gene editing, and treatments for diseases once thought incurable.
Scientists at the University of Hong Kong have developed a breakthrough tool that can repair faulty genetic messages in living cells without permanently changing DNA. The innovation could transform treatment for diseases like Huntington's by removing harmful RNA segments while keeping the healthy parts intact.
A 19-year-old from British Columbia became the first person ever cured using "prime editing," a breakthrough gene therapy that fixed a fatal immune disorder. The treatment freed him from daily medication and the constant fear of life-threatening infections.
Scientists have developed a new gene editing approach that spreads healing changes from cell to cell, dramatically increasing its reach in the body. This breakthrough could transform treatment for countless genetic diseases that were previously too difficult to address.
Scientists are developing a breakthrough gene editing approach that spreads between cells like neighbors sharing flyers. This could treat far more diseases by reaching dramatically more cells in the body.
University of Virginia researchers used gene editing to fix the DNA mutation causing a deadly form of epilepsy, potentially opening the door to cures for inherited brain disorders. The technique eliminated seizures in lab mice and improved their movement and cognitive function.
Scientists prevented a life-threatening brain condition in newborn mice using RNA therapy, reducing cases by 67%. The breakthrough could spare thousands of babies from risky brain surgery each year.
Scientists created a 45-unit RNA molecule that can almost replicate itself, bringing us closer to understanding how life began on Earth. This tiny strand performs both key steps needed for self-replication, just not yet in the same container.
Australian researchers developed an AI system that makes gene editing safer by protecting healthy genes during treatment. The breakthrough could transform how doctors treat genetic diseases like cystic fibrosis.
Scientists are calling new gene editing treatments a potential "functional cure" for sickle cell disease, offering hope to millions. Early results show patients living pain-free after a single treatment.
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After a deadly fungus wiped out billions of American chestnut trees, scientists are using gene editing to bring them back. Three new approaches could also save coral reefs, black-footed ferrets, and other threatened species.
Scientists created wheat that produces up to 93% less of a toxic compound when toasted, potentially making your morning toast much safer. The breakthrough uses precise gene editing without reducing crop yields.
Australian researchers discovered an RNA molecule that destroys the most common type of breast cancer while leaving healthy cells untouched. The breakthrough could lead to new treatments for women whose cancer no longer responds to existing drugs.
An 18-year-old patient with a once-incurable immune disease now shows no symptoms after Montreal doctors used groundbreaking "prime editing" gene therapy. A year after treatment, he's living a normal life with three-quarters of his diseased cells permanently corrected.
Scientists from Harvard, MIT, and Case Western used CRISPR gene editing to extend the lives of mice with deadly prion diseases by 60%. While the treatment isn't ready for humans yet, it marks a breakthrough against diseases that currently have no cure.
A bacterial defense system discovered in 2012 has transformed into life-saving treatments for cancer and rare diseases. Scientists refined CRISPR gene editing from crude molecular scissors into precision medicine that's curing patients today.
A one-time gene-editing treatment slashed bad cholesterol by 62% in early human trials, offering hope for millions who struggle with heart disease prevention. Eli Lilly's breakthrough therapy showed no serious side effects in the study.
Ty Sperle, 18, became the first person in the world cured of chronic granulomatous disease through groundbreaking gene editing treatment. His success opens the door for curing countless other rare genetic diseases affecting children everywhere.
A groundbreaking RNA therapy just succeeded in early trials for a rare muscular dystrophy affecting thousands, and it could become the first treatment that actually modifies the disease's progression. Novartis's del-brax showed clear signs of reducing muscle damage in patients with facioscapulohumeral muscular dystrophy.
A one-time gene-editing treatment just became the first to succeed in a major clinical trial, reducing dangerous swelling attacks by 87% for people with a rare genetic condition. The breakthrough could change what's possible for treating genetic diseases.
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